How your gift powers treatment
Your donation is not funding hope someday. It is funding life-changing treatment now—before Ivy’s developmental window closes. As shown in the examples below, every contribution funds a concrete step in n-Lorem’s proven pathway for creating personalized ASO treatments.
And the impact of your donation doesn’t stop there. n-Lorem’s success on Ivy’s case will benefit other patients with similar ultra-rare mutations, helping those who come after her get treated faster.
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$250
Fund one hour of an n-Lorem scientist working on Ivy’s case
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$1,000
Power small-scale synthesis of one candidate ASO in n-Lorem’s lab
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$5,000
Conduct an 8-week tolerability study of one candidate ASO in rats
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$10,000
Support one of several critical safety tests on the final ASO
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$60,000
Fund GMP manufacturing of the final ASO
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$150,000
Advance the last step: placing the final ASO in sterile vials and sealing them for transport to Ivy’s doctor